Vamorolone vs corticosteroid real-world experience: Comparisons of 2-year treatment with NorthStar UK Network and CINRG Duchenne Natural History Study

Author(s):

Jean Mah, MD, MS, Alberta Children's Hospital Research Institute, University of Calgary, Calgary, Alberta, Canada, Paula R. Clemens, MD, University of Pittsburgh School of Medicine, VA Pittsburgh Healthcare System, Pittsburgh, PA, USA, Michela Guglieri, MD, John Walton Muscular Dystrophy Research Centre, Newcastle University, Newcastle upon Tyne, UK., Edward Smith, MD, Duke University Hospital, Richard Finkel, MD, St. Jude Children’s Research Hospital, Memphis, TN, USA., Mar Tulinius, MD, Queen Silvia Children’s Hospital, Gothenburg, Sweden., Yoram Nevo, MD, Schneider Children’s Medical Center, Tel Aviv University, Tel Aviv, Israel., Monique Ryan, Dr, Murdoch Children's Research Institute, Richard Webster, MD, The Children’s Hospital at Westmead, Sydney, Australia., Diana Castro, MD, University of Texas Southwestern, Dallas, TX, USA., Nancy Kuntz, MD, Ann & Robert H. Lurie Children’s Hospital, Chicago, IL, USA., Craig McDonald, MD, UC Davis Health, Georgia Stimpson, MS, Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK., Deborah Ridout, MS, Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK., Vandana Ayyar-Gupta, PhD, Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK., Giovanniu Baranello, MD, Dubowitz Neuromuscular Centre, UCL Great Ormond Street Institute of Child Health, London, UK., Adnan Manzur, FRCPCH, Great Ormond Street Institute of Child Health, London, UK, Francesco Muntoni, MD, Great Ormond Street Institute of Child Health, London, UK, Leanne Ward, MD, Children’s Hospital of Eastern Ontario, Ottawa, ON, Canada., Heather Gordish-Dressman, PhD, Children’s National Hospital, Washington DC, USA., Eric Hoffman, PhD, AGADA Biosciences Inc., Utkarsh Dang, PhD, Carleton University, Ottawa, ON, Canada.