Association Between Glucocorticoid Treatment Duration and Healthcare Resource Utilization in Duchenne Muscular Dystrophy: A Real-World Analysis


Topic:

Other

Poster Number: 75 S

Author(s):

Steven Woods, PharmD, Catalyst Pharmaceuticals, Bridget McGowan, MD, Ann and Robert H. Lurie Children's Hospital of Chicago, Ashley Martin, PhD, BluePath Solutions, Alexa Gordon, MS, BluePath Solutions, Sana Mirza, MPH, BluePath Solutions, Paula Alvarez, MBA, MS, Rph, Critical Intelligence Consulting

Objective: Glucocorticoids (GCs) are standard treatment in Duchenne muscular dystrophy (DMD) but may increase healthcare resource utilization (HCRU) due to treatment-related adverse outcomes. This study examined the association between GC duration and HCRU in a real-world US cohort.

Methods: This retrospective cohort study used 2017–2022 Medicaid claims data for male DMD patients aged ≤30 years, grouped by GC duration: <20, 20–60, or >60 months. HCRU outcomes included inpatient admissions (including length of stay [LOS]), emergency room (ER), and outpatient visits, classified as GC- or non-GC-related. Regressions estimated HCRU, adjusting for age, race/ethnicity, Charlson Comorbidity Index, duration of follow-up, and GC switching. Adverse outcomes were summarized descriptively to contextualize outpatient utilization.

Results: Among 1,365 male DMD patients (mean age 11.6 years; mean GC use 45.5 months), mean LOS for GC-related inpatient admission was 11.0 days (<20), 9.2 (20–60), and 7.6 (>60); mean ER visits were 6.3, 4.8, and 5.2, respectively. Adjusted results found inpatient and ER utilization did not significantly differ by GC duration. GC-related outpatient visits increased with duration (8.2 vs. 10.6 vs. 14.5; p < 0.001) but represented a small portion of utilization. Notable GC-related outcomes—including infections, fractures, and cataracts—were observed with increasing rates across duration groups. Non-GC-related visits reflected hallmark DMD manifestations and the overall burden. Conclusion: While traditional GCs remain central to DMD care, longer use is associated with increased outpatient burden driven by both disease progression and treatment-related effects. These findings highlight the need for therapies that reduce overall disease burden and HCRU.